Pediatric specialists, evaluate children with genetically defined, primary immune defects that lead to recurrent serious infection in childhood and adolescents. For these patients, bone marrow transplant or gene therapy, where appropriate, are used for immune reconstitution.

Treats diseases for which bone marrow(stem cell) transplantation has been curative, such as : leukemia myelodysplastic syndrome (MDS), sever aplastic anemia, inherited bone marrow failure syndromes, brain tumors, sickle cell anemia, thalassemia, immunodeficiency disorder, and metabolic storage diseases.

Maintains computer registry of volunteer marrow donors and conducts searches for unrelated marrow donors for patients in need of bone marrow transplant. Patient Advocacy Office helps patients with information about matching, unrelated donors, financing a transplant, and choosing a transplant center.

Offers individuals who have had bone marrow or stem cell transplant surgery the opportunity to interact with their peers, share concerns and successes.

Provides information and referral, education, and telephone support to people dealing with bone marrow transplants.